Los ensayos clínicos son estudios médicos en los que participan personas con determinadas características necesarias para ayudar a hallar nuevas formas que sean seguras y eficaces para prevenir, detectar o tratar enfermedades o condiciones.

• Buscador de Ensayos clínicos https://clinicaltrials.gov/
• Propel – Brigebio QED Therapeutics https://bridgebio.com/news/bridgebio-announces-first-child-dosed-with-infigratinib-in-propel-3-its-phase-3-clinical-trial-in-children-with-achondroplasia
• ACcomplisH Trial of TransCon CNP – Ascendis Pharma https://investors.ascendispharma.com/news-releases/news-release-details/data-phase-2-accomplish-trial-transcon-cnp-children 
• FGFR3 – Tyra https://tyra.bio/pipeline/ 
• SAR442501 – Sanofi https://www.rarediseases.sanofimedical.com/dam/jcr:1ee59eb5-4d0a-49ca-be8e-130eb99455f8/Rare-Disease-Pipeline-Overview.pdf